09/18/2026
Today the FDA approved the first gene therapy treatment for Sanfilippo Syndrome Type A. The work on this has been long and the joy in the community is so rich. The team at Wave therapies is thankful for being part of care for several kids in this community and shares the bitter sweet of a joyous moment while remembering those lights that we have lost. And for the families with Type B - we continue standing with you while the science continues working for your families. The journey continues.