BioMarin Pharmaceutical Inc.

09/02/2026

Fashion, friendship and her beloved cat Pati are at the heart of Aslim’s world. The 18-year-old from Ankara, Türkiye recently graduated from high school and dreams of becoming a famous fashion designer. She spends her time sketching women’s clothing designs.

“My designs make me happy when they go out into the world,” Aslim shares.

Aslim lives with (MPS) type IVA, also known as Morquio A syndrome, a progressive, rare genetic condition that causes the buildup of complex carbohydrates in the body and can lead to complications affecting multiple organs. While her family noticed symptoms when she was young, including changes in her vision, it took four years before she received an official diagnosis at age 7.

When the diagnosis finally came, it brought both answers and a path forward. Aslim’s mother, a physician, quickly sought the support and care her daughter needed, while the whole family rallied around her.

“Whenever I felt tired, my dad would carry me and pretend I was flying,” she recalls.

Today, Aslim uses a wheelchair, which she names after her favorite superheroes.

“I have three wheelchairs: Morgana, my first wheelchair, which is now retired after eight years; Shuri, my day-to-day chair; and Ramonda,” she says “They're all female superheroes who inspire me.”

Beyond her family, Aslim has also found a sense of belonging through the MPS community. Through local and international WhatsApp groups, she has built meaningful friendships with others living with MPS and found comfort in connecting with people who understand her experiences. Aslim especially enjoys encouraging others who are navigating life with MPS.

“When someone comes to me and asks how to get through it, I feel like a big sister,” she says.

Looking ahead, Aslim hopes to build a successful career in fashion while continuing to advocate for the MPS community around the world. By sharing her story, she hopes other people living with MPS know they are not alone and that their dreams remain possible.

“I want people, especially doctors, to understand that they shouldn't make assumptions,” she says. “MPS affects us all differently, so listen to us.”

For families and individuals navigating a new diagnosis, she offers a message of hope.

“It’s going to be okay, one way or another,” she says. “Even if you don't feel love or support right now, somewhere in the world, someone is cheering you on.”

08/27/2026

Jacob has always dreamed big. A recent high school graduate who is living with achondroplasia, he is beginning his aerospace engineering journey at UC Merced with hopes of one day working for NASA.

Along the way, Jacob has faced nearly 40 surgeries, built confidence through family, mentors and JROTC, and stayed focused on what drives him forward: curiosity, perseverance and possibility.

His grandmother, Annette, turned that belief into "Jacob’s Big Dream," a children’s book inspired by his story.

Through BioMarin’s Making Space series, we’re proud to share stories like Jacob’s that remind us potential is not defined by a diagnosis, and that dreams grow with support, belief and opportunity.

Read more: http://ms.spr.ly/6181auW3c

08/25/2026

Ben Schooler has experienced the full arc of biopharmaceutical science – from bench to delivering life-changing medicines to people with rare genetic conditions. Since joining BioMarin more than 18 years ago, Ben has worn many hats: advancing research, leading lab operations and now focusing on strategy within Technical Operations.

“What drives me is bringing those perspectives together,” Ben says. “Understanding the science, the operational realities and the big-picture strategy – while never losing sight of why we do this work.”

Read more about Ben’s journey, the connections that inspire him and why he believes operational strategy can be just as meaningful as scientific discovery: http://ms.spr.ly/6183aPn8t

08/21/2026

All of us at BioMarin want to thank and recognize Terri Klein for her incredible leadership these past decades. Terri has been a wise and passionate advocate for the MPS community, as well as an amazing partner to us and so many others. Congratulations on this transition Terri, and on the legacy you have built. Thank you.

After 18 years of dedicated leadership, Terri Klein, President & CEO of the National MPS Society, will conclude her service on December 31, 2026.

Terri has championed family support, strengthened community partnerships, and helped advance newborn screening, research, treatment development, and advocacy for MPS and ML. She also grew the Pathways Program and brought the International MPS Registry to the Society.

"Serving this extraordinary community for the past 18 years has been one of the greatest privileges of my life," said Klein.

The Board will launch a national search for the Society's next President & CEO.

Read the full announcement: https://mpssociety.org/en/news/klein-2026-announcement/

Thank you, Terri, for your unwavering commitment to the MPS and ML community. 💜

08/20/2026

Last week, our showcased the projects, insights and experiences that shaped their time at BioMarin during intern poster fairs around the globe.

Many of our more than 100 interns came together to present the key learnings and achievements from their various summer projects. With presentations ranging from scientific discovery to AI, quality, engineering and business innovation, interns highlighted their impact and reflected on a summer of learning, growth and collaboration.

Thank you to the mentors, managers and colleagues who helped make these experiences possible. We're proud of all that our interns have accomplished and excited to see what comes next.

08/19/2026

Samat has dedicated his life to helping others. The 37-year-old from Kazakhstan is a teacher in an onco-hematology department, a hospital clown who brings smiles to children during difficult moments and the leader of the Zhana Omyr foundation, supporting people living with MPS and other rare conditions. Beyond his work, Samat says his greatest joy comes from spending time with his wife, Nurgul, and their daughter, Aisha.

“Nurgul is always there for me, supporting me, understanding me and helping me through every situation in life,” Samat says.

Samat lives with (MPS) type II, a rare genetic condition also known as Hunter syndrome that causes the buildup of complex sugars in the body, which can lead to complications affecting multiple organs and systems.

As a child, Samat remembers being one of the tallest students in his class before his growth suddenly slowed. Instead of letting that discourage him, he spent five years training in Greco-Roman wrestling, an experience that strengthened both his confidence and resilience.

One of the most meaningful parts of Samat's journey has been his connection to the MPS community and the sense of purpose his foundation provides.

“I realized that I was not alone with this condition,” he says. “Later I found out that I am one of the oldest people living with MPS II, and I became an example for children and support for their parents.”

Today, Samat channels that experience into advocacy. As a member of the Board of Directors for the IMPS Network, he works to raise awareness of rare conditions and promote the importance of early diagnosis.

“I accepted the MPS II diagnosis as part of my life,” he says. “It did not become a limitation. On the contrary, it gave me inner strength and an understanding of how important it is to keep moving forward.”

Looking ahead, Samat hopes more families affected by MPS will have access to the knowledge and support they need to thrive.

“It is very important that society, especially doctors, have a better understanding of what MPS is," he says. “Awareness and timely diagnosis play a key role in patients' lives.”

08/17/2026

Every child's experience with hypochondroplasia is unique, but many families share a need for clear information, practical guidance and support.

That’s why we’ve launched "Hypochondroplasia: The Inside Story," a new online resource hub designed for families navigating this form of skeletal dysplasia that can impact growth, development and overall health.

The site offers education about hypochondroplasia, information about care and management, and community-informed tips and resources to help families make care decisions with greater confidence.

Visitors can also sign up to stay informed about events and resources designed to help connect and support the hypochondroplasia community.

Visit the website to learn more: http://ms.spr.ly/6188aKtDQ

08/13/2026

We’re proud to sponsor the second year of Camp Ellellbee, a family camp launched by The Little Legs Big Heart Foundation to help foster community and provide support to people living with skeletal conditions and their families.

Camp Ellellbee sessions in California and Georgia are full, but limited openings remain for people interested in attending the Maine, Texas and Utah camps.

Camp Sunshine in Casco, Maine (Aug. 28-30)

Camp for All in Burton, Texas (Oct. 2-4)

National Ability Center in Park City, Utah (Oct. 16-18)

Learn more and register today: http://ms.spr.ly/6188ayqxq

08/12/2026

The BioMarin Women’s Alliance (BWA) Employee Resource Group (ERG) recently brought colleagues together at our San Rafael headquarters to celebrate the recipients of this year’s BWA Champion Awards.

Selected from nearly 100 nominations submitted by colleagues around the world, this year’s 19 winners reflect the many ways our employees support, empower and inspire one another. Congratulations to Erin Koek, Gol Newall, Ioanna Ntai, Janine Ilagan and Natalia Kazimi for mentorship; Emma Christine O’Leary, Jill Wait, Kate Creedon, Martine Avello and Shanika Livingston for community building; Fabiola Spila, Ken Reilly, Matt Morrow, Niamh Ferguson and Prarthana Patil for allyship; and Deepika Vaidyanathan, Nicola Fowler, Noelle Thompson and Vanessa Abe for women’s well-being.

Thank you to BWA – particularly to Audrisz Asuncion for leading the event – and to everyone who submitted nominations. Together you helped shine a light on colleagues whose leadership, support and commitment strengthen our global community.

08/11/2026

Cristin Hubbard is still motivated by the same idea that sparked her earliest interest in healthcare and eventually led her to biopharma: getting medicines to the people who need them most.

At BioMarin, Cristin says she feels the impact of that commitment as strongly as ever.

“What I love about working in rare disease is the connection to the communities we serve,” says Cristin, BioMarin’s Chief Commercial Officer. “You feel like every contribution matters so deeply for patients and their families.”

From early work as a medicinal chemist to leading global commercial teams, her career has been shaped by a consistent focus on bringing innovation closer to patients. She’s applying those experiences to help BioMarin leverage its global footprint and capabilities and ultimately reach more people living with rare genetic conditions around the world.

We sat down with Cristin to reflect on her professional journey, her leadership philosophy and how her experience across a variety of roles has prepared her for this moment at BioMarin.

Read more in the full interview: http://ms.spr.ly/6184aHZPq